Niemann-Pick disease type C1

Active Research Protocols

  1. 09-CH-0185 – Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine
  2. 13-CH-0001 – Intracerebroventricular 2-Hydroxypropyl-B-Cyclodextrin in Patients with Niemann-Pick Disease, Type C1
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This page was last updated: January 24, 2014